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Andrea Alms Video:  Money In Motion 157 - Disruption In The Gene Cell Therapy Market

May 2025 - Private Equity

posted by BrookDell Partners

Andrea Alms Video: Money in Motion 157 - Disruption in the Gene Cell Therapy Market


TRANSCRIPT:   Hello, my name is Andrea Alms. I'm a technology investor and financial manager and this is your money in motion. In the news selling gene therapy reckoning industry giants retreat as safety concerns and regulatory shifts reshape the landscape. Vertex, Pfizer, Takeda are leaving the AAV gene medicine research. The manufacturing economics are challenging a 2 to $3 million per dose and safety events, and suddenly the risk benefit calculus looks radically different.


In addition to the Trump administration creating great uncertainty in the market and in the regulatory entities. What is AAV? In an earlier episode, I reported on the advertisement. Associated virus gene therapy is important as it is a leading platform for delivering genes to treat various diseases. It is intended to correct the genetic defect that causes the disease. Averaging the averages.


The global market is $4.1 billion and at a 23.1% growth rate, the great technology rotation non viral approaches gain momentum. The winners in this new landscape, according to industry strategists, will be teams that successfully pivot from the initial genetic jet AAV vectors to modular, non-viable systems, building manufacturing processes robust enough to pass increasingly stringent regulatory scrutiny and develop reimbursement approaches aligned with outcome based models. Thank you. This is your money. Your money in motion.




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ALL ALPHAMAVEN CONTENT IS FOR INFORMATIONAL PURPOSES ONLY. CONTENT POSTED BY MEMBERS DOES NOT NECESSARILY REFLECT THE OPINION OR BELIEFS OF ALPHAMAVEN AND HAS NOT ALWAYS BEEN INDEPENDENTLY VERIFIED BY ALPHAMAVEN. PAST PERFORMANCE IS NOT INDICATIVE OF FUTURE RESULTS. THIS IS NOT A SOLICITATION FOR INVESTMENT. THE MATERIAL PROVIDED HEREIN IS FOR INFORMATIONAL PURPOSES ONLY. IT DOES NOT CONSTITUTE AN OFFER TO SELL OR A SOLICITATION OF AN OFFER TO BUY ANY INTERESTS OF ANY FUND OR ANY OTHER SECURITIES. ANY SUCH OFFERINGS CAN BE MADE ONLY IN ACCORDANCE WITH THE TERMS AND CONDITIONS SET FORTH IN THE INVESTMENT'S PRIVATE PLACEMENT MEMORANDUM. PRIOR TO INVESTING, INVESTORS ARE STRONGLY URGED TO REVIEW CAREFULLY THE PRIVATE PLACEMENT MEMORANDUM (INCLUDING THE RISK FACTORS DESCRIBED THEREIN), THE LIMITED PARTNERSHIP AGREEMENT AND THE SUBSCRIPTION DOCUMENTS, TO ASK SUCH QUESTIONS OF THE INVESTMENT MANAGER AS THEY DEEM APPROPRIATE, AND TO DISCUSS ANY PROSPECTIVE INVESTMENT IN THE FUND WITH THEIR LEGAL AND TAX ADVISERS IN ORDER TO MAKE AN INDEPENDENT DETERMINATION OF THE SUITABILITY AND CONSEQUENCES OF AN INVESTMENT.